A Phase 3, Double-blind, Randomized, Placebo-Controlled, Multicenter Study Evaluating the Efficacy and Safety of Mitapivat in Subjects With Non–Transfusion-Dependent Alpha or Beta Thalassemia (ENERGIZE)
Phase 3 – large-scale trial before approval
Conditions:
Non–Transfusion-Dependent Alpha- or Beta-Thalassemia
Sponsor: Agios Pharmaceuticals Inc.
trial.available_in:
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Overview
Trial status: Authorised
Hemoglobin (Hb) response, defined as a ≥1.0 g/dL increase in average Hb concentration from Week 12 through Week 24 compared with baseline
Who can participate
Age group: 18-64 years, 65+ years
Gender: Female, Male
Target enrollment: 86 participants
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