BONAPH1DE, A Prospective Observational Study of Patients With Primary Hyperoxaluria Type 1 (PH1)
Заболявания:
Primary Hyperoxaluria Type 1
Спонсор: Alnylam Pharmaceuticals
Налично на:
БГ
Обобщение
The purpose of this study is to describe the natural history and progression of patients diagnosed with PH1, and to characterize the long-term real-world safety and effectiveness of lumasiran.
Кой може да участва
Inclusion Criteria:
* Documented diagnosis of PH1, per physician's determination
Exclusion Criteria:
* Currently enrolled in a clinical trial for any investigational agent