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Active (not recruiting) NCT04982393

BONAPH1DE, A Prospective Observational Study of Patients With Primary Hyperoxaluria Type 1 (PH1)

Conditions: Primary Hyperoxaluria Type 1

Sponsor: Alnylam Pharmaceuticals

trial.available_in: БГ
Overview
The purpose of this study is to describe the natural history and progression of patients diagnosed with PH1, and to characterize the long-term real-world safety and effectiveness of lumasiran.
Who can participate
Inclusion Criteria: * Documented diagnosis of PH1, per physician's determination Exclusion Criteria: * Currently enrolled in a clinical trial for any investigational agent
Locations 30
Belgium (2)
Clinical Trial Site
Ghent
Clinical Trial Site
Liège
Canada (3)
Clinical Trial Site
Hamilton , Ontario
Clinical Trial Site
Laurier , Quebec
Clinical Trial Site
Toronto , Ontario
France (3)
Clinical Trial Site
Bordeaux
Clinical Trial Site
Lyon
Clinical Trial Site
Paris
Germany (3)
Clinical Trial Site
Berlin
Clinical Trial Site
Cologne
Clinical Trial Site
Hamburg
Israel (1)
Clinical Trial Site
Jerusalem
Italy (3)
Clinical Trial Site
Milan
Clinical Trial Site
Orbassano , Torino
Clinical Trial Site
Verona
Netherlands (1)
Clinical Trial Site
Amsterdam
Spain (3)
Clinical Trial Site
Barcelona
Clinical Trial Site
Las Palmas
Clinical Trial Site
Santa Cruz de Tenerife , Canary Islands
Switzerland (1)
Clinical Trial Site
Bern
United Kingdom (2)
Clinical Trial Site
London , England
Clinical Trial Site
London
United States (8)
Clinical Trial Site
Boston , Massachusetts
Clinical Trial Site
Cincinnati , Ohio
Clinical Trial Site
Dallas , Texas
Clinical Trial Site
Houston , Texas
Clinical Trial Site
Phoenix , Arizona
Clinical Trial Site
Pittsburgh , Pennsylvania
Clinical Trial Site
Rochester , Minnesota
Clinical Trial Site
Washington D.C. , District of Columbia
Technical details
Status
Active (not recruiting)
Study type
OBSERVATIONAL
Sex
Male and female
Healthy volunteers
No
Start date
13.12.2021
Completion date
01.09.2028
Registry ID
NCT04982393
Source
clinicaltrials.gov
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